Learning center

Learning about gene therapy can feel complex in the beginning. Take it one step at a time and remember that Vertex is here to provide helpful resources for your educational journey.

Talk to your doctor if you have specific questions.

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GenePossibilities provides resources to help you explore gene therapy. Use these resources to educate yourself and help guide potential conversations with your doctor, support system, and community.

Discover gene therapy

Learn more about gene therapy, the different types and methods, and the possibilities it holds for people living with genetic diseases.

Explore approaches

Learn more about gene editing and gene addition, 2 types of gene therapy currently under investigation for treating genetic diseases.

Learn about the CRISPR/Cas system

Learn about the CRISPR/Cas system, a type of gene editing. Review the system and how it works to address disease.

Start the conversation

Learn how to start conversations about the gene-therapy treatment journey with your doctor.

Resources to aid in your journey

You will find more information on gene therapy in various articles and other resources. Check back periodically as we will continue to add more resources.

Helpful articles and links

Different approaches—American Society of Gene & Cell Therapy (ASGCT)

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Gene therapies—National Heart, Lung, and Blood Institute

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National Organization for Rare Disorders (NORD) expands gene therapy offerings through new online resources

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Advocacy organizations

To start learning about gene therapy, it’s important to start with a strong foundation. Go back to the beginning and start your journey by learning all about genes.

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